ZFN-mediated in vivo gene editing in hepatocytes leads to supraphysiologic α-Gal A activity and effective substrate reduction in Fabry mice - ScienceDirect
ZFN-mediated in vivo gene editing in hepatocytes leads to supraphysiologic α-Gal A activity and effective substrate reduction in Fabry mice - ScienceDirect
ZFN-mediated in vivo gene editing in hepatocytes leads to supraphysiologic α-Gal A activity and effective substrate reduction in Fabry mice - ScienceDirect,ZFN-mediated in vivo gene editing in hepatocytes leads to supraphysiologic α-Gal A activity and effective substrate reduction in Fabry mice - ScienceDirect,Fabry Enzyme Replacement Therapy ISU303 Shows Promise: Trial | ISU Abxis Therapy Shows Efficacy, Good Safety Profile in Patients | Fabry Disease News,Critical roles of FAM134B in ER-phagy and diseases | Cell Death & Disease,Critical roles of FAM134B in ER-phagy and diseases | Cell Death & Disease,